Detalhe da pesquisa
1.
Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria.
N Engl J Med
; 382(24): 2289-2301, 2020 06 11.
Artigo
Inglês
| MEDLINE | ID: mdl-32521132
2.
Phase 1 Trial of an RNA Interference Therapy for Acute Intermittent Porphyria.
N Engl J Med
; 380(6): 549-558, 2019 02 07.
Artigo
Inglês
| MEDLINE | ID: mdl-30726693
3.
EXPLORE: A Prospective, Multinational, Natural History Study of Patients with Acute Hepatic Porphyria with Recurrent Attacks.
Hepatology
; 71(5): 1546-1558, 2020 05.
Artigo
Inglês
| MEDLINE | ID: mdl-31512765
4.
Data-driven epidemiologic approach to conducting site feasibility for a global phase III tuberculosis vaccine clinical trial.
PLOS Glob Public Health
; 3(11): e0002544, 2023.
Artigo
Inglês
| MEDLINE | ID: mdl-37939024
5.
Patient Perspective on Acute Intermittent Porphyria with Frequent Attacks: A Disease with Intermittent and Chronic Manifestations.
Patient
; 11(5): 527-537, 2018 10.
Artigo
Inglês
| MEDLINE | ID: mdl-29915990